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Pipeline

Pipeline

Developing promising new therapies for patients with rare genetic diseases.

BioMarin is actively pursuing strategies to enhance its exciting product portfolio. The company has a growing product pipeline, with multiple clinical and nonclinical IND (Investigational New Drug) candidates in development.

Click on the pipeline to learn more about each product candidate.

Naglazyme for MPS VI Aldruazyme for MPS I PEG-PAL for PKU Morquio-Syndrome BMN-195-Utrophin-Inducer-for-Duchenne-Muscular-Dystrophy BMN-185-IgA-Protease-for-Nephropathy Kuvan for PKU